Metagenomi Therapeutics Inc

Metagenomi Therapeutics, Inc. is a precision genetic medicines company, which engages in the business of developing next generation gene-editing technologies and therapies. The company is headquartered in Emeryville, California and currently employs 113 full-time employees. The company went IPO on 2024-02-09. The company discovers and develops a suite of novel editing tools potentially capable of correcting any type of genetic mutation found anywhere in the human genome. The company focuses on value programs in disease indications with well-understood biology and clearly defined clinical development and regulatory pathways. Its lead candidate, MGX-001, is a wholly-owned development program in hemophilia A, has demonstrated a preclinical profile potentially competitive with treatment options, including targeted genome editing and durable gene expression in a one-time treatment. MGX-001 is designed to provide curative, life-long protection from bleeding events and joint damage in adults and children with hemophilia A. MGX-001 is designed to insert a Factor VIII (FVIII) DNA cassette into a safe harbor location within an intron of the albumin gene.